This years All Info - H.Res.181 - 118th Congress (2023-2024): Expressing WebLeveraging the momentum for a comprehensive rare disease strategy The 3rd International Conference on Rare Diseases organized by Rare Diseases Greece (RDG), 95 Rare Rare Disease Conference 2023 Upcoming Events National Organization for Rare October 1, 2022Deadline for submission of full-length manuscripts for peer-review in the Lysosomes issue of Molecular Genetics & Metabolism, February, 2023. Google Calendar iCalendar Outlook 365 Outlook Live Details Date: February 27 Time: 9:00 am - 4:45 pm EST Event Category: NORD Sponsored Rare Disease Day Event Website: Before sharing sensitive information, make sure you're on a federal government site. After reviewing numerous nominations, and considering many amazing individuals, the WORLDSymposium2023 Awards Committee has selectedWilliam A. Gahl, MD, PhD, as the recipient of the2023 Roscoe O. Brady Award. May 23-25, 2023 Gaylord National Resort & Convention Center Washington, D.C. To register for On Demand, click here, and then click Already Registered? to modify your registration or click Register to access this content. Save the date for NORD Summit 2023, set for October 16-17, 2023 in Washington, DC! Identify pertinent evolution of Health technologies in RARE DISEASES fields. Youll have opportunities to learn quickly, advance your career, and to meaningfully impact our customers and our business. Initiate a mutually beneficial dialogue among the rare diseases community. WORLDSymposium receives NO FUNDING of any kind from the LDN, the National Institutes of Health (NIH), or any other federal agency. T: (+1) 617 455 4188 WORLDSymposium is excited to announce the return of Peter Marks, MD, PhD, director of the Center for Biologics Evaluation and Research (CBER) at the Food and Drug Administration, as the 2023 Keynote Speaker. Rare Diseases Conferences I was able to watch a little in person and then I was able to access NORDs session files. WORLDSymposiumwas pleased to announce the recipients of the 2023 New Treatment Award. Join the webcast to watch the livestream on February 27 beginning at 9 a.m. (ET). 500+ leading experts from innovative biotechs, large pharma, academia and key service providers will be reuniting in Boston for 2023 to capitalize on recent success stories and collaborate over the most pressing industry challenges. By RoundTables. Our mission is to promote inter-professional healthcare education and awareness of and , Continue reading "2023 Rare Disease Day Symposium at the Frank H. Netter MD School of Medicine", 1900 Crown Colony Drive Suite 500 Download the presentation, Mari MUREL, ERICA Project Manager Engage with the FDA to provide your perspectives as a patient, caregiver or family member. WebRare Disease Day will be taking place on March 24, 2023 at 5:00 PM (ET). Christine founded the Cure GM1 Foundation in April 2015 in honor of her daughter Iris and all those affected by GM1 gangliosidosis. Conferences Rare Diseases Join the webcast to watch the livestream on February 27 beginning at 9 a.m. (ET). International Conference Rare Diseases and its Treatment aims to bring together leading academic scientists, researchers and research scholars to exchange and share their experiences and research results on all aspects of Rare Diseases . 2022 has been a landmark year for the global gene therapy space. Marriott Marquis in Washington, DC, NORD Leads the Way: 900+ Influential Rare Disease Stakeholders from FDA, Patient Organizations, and Industry Gather for #NORDSummit 2023. 1140062 and a company registered in England and Wales no. With NCATS' Division of Rare Diseases Research Innovation (DRDRI) facilitates and coordinates NIH-wide research activities, which have the potential to speed development of treatments for multiple rare diseases and ultimately help more patients more quickly. Presentations. FDA will host Rare Disease Day, a virtual public meeting, on February 27, 2023, 9:00 am 4:45 pm ET, in global observance of Rare Disease Week. November 18, 2022 Registration is now open for the 2023 Muscular Dystrophy Association (MDA) Clinical & Scientific Conference focusing on neuromuscular diseases, including Duchenne muscular dystrophy (DMD), spinal muscular atrophy (SMA), myasthenia gravis, and Pompe disease, among others. WebThe joint event RE(ACT) Congress and IRDiRC Conference 2023 aims to bring together scientific leaders and experts and young scientists from various breakthrough scientific fields to present cutting-edge research, exchange ideas, and discuss rare diseases research policies. WebMarketsandMarkets Infectious Disease and Molecular Diagnostics Conference 22nd - 23rd June 2023 Boston, USA The Diagnostics sector has emerged as a prominent game changer in healthcare, because of many technological advancements taking February 13, 2023 Speaker and Abstract Submissions Open, March 10, 2023 Speaker Submission Deadline, March 15, 2023 Scholarship Application Window Opens, September 5, 2023 Early Bird Registration Closes, July 14, 2023 Abstract Submission Deadline, August 15, 2023 Abstract Decision Notifications by NORD, September 22, 2023 Hotel Room Block Closes, October 15, 2023 NORD Rare Diseases & Orphan Products Breakthrough Summit Welcome Reception, October 16 -17, 2023 NORD Rare Diseases & Orphan Products Breakthrough Summit, What an incredible lineup of speakers. 3RD INTERNATIONAL RARE DISEASES CONFERENCE 2023: We are looking forward to gathering in person for Rare Disease Day 2023 on February 25th starting at 9:00 am at the Prince Conference Center (Grand WORLDSymposia - We're Organizing Research on WORLDSymposium is managed by GMI, Inc. and Saterdalen & Associates, LLC. August 1, 2022Registration for the conference opens. The site is secure. February 21, 2023: Robert J. Gorlin Symposium and Emerging Trends, Hilton Orlando6001 Destination ParkwayOrlando Florida, USA, 32819Phone: +1-407-313-4300Website: hilton.comWebsite: thehiltonorlando.com. Demonstrate the NIH commitment to helping people with rare diseases through research. Thank you for the opportunity to present on the vitally important topic of transition of care., NEMSNs Board thanks you very kindly for your scholarship to our organization to attend the 2020 Rare Summit. Assess and understand application challenges with current technology features. The Francis Crick Institute Limited is a registered charity in England and Wales no. Rare Disease WebVideo: Rare Disease Day Conference 2023 | Akron Children's Hospital. This free family-friendly BBQ will feature live music, a kid's zone, food trucks, educational resources, and more! Learn more about how you can attend this event or add it to your calendar. Volunteer. Rare Disease Most of these people are children. Each year, WORLDSymposium hosts a scientific meeting presenting the latest information from basic science, translational research, and clinical trials for lysosomal diseases. NORD at UVA Speaker Panel 2023 . Session: R&D Spotlight - Rare Disease Date: Tuesday, April 25, 2023 Time: 4:00 p.m. - 5:15 p.m. Greenwich Mean Time Venue: ETC Venues, 155 Bishopsgate, London, England EC2M 3YD About BioTrinity BioTrinity is a London conference that catalyzes growth and supports in-person re-engagement across the life sciences industry. The conference seeks to contribute to presenting novel research results in all aspects of Rare Diseases and Orphan Drugs. Rare diseases often are difficult to diagnose it can take years. The 6th Annual Gene Therapy for Rare Disorders 2023 Summit remains devoted to showcasing the top case studies and strategic learnings from the past year. After reviewing numerous nominations, and considering many amazing individuals, the WORLDSymposium 2023 Awards Committee has selected Christine as the recipient of the 2023 PAL Award. Appraise and qualify unmet needs from clinician users. WebThe joint event RE(ACT) Congress and IRDiRC Conference 2023 aims to bring together scientific leaders and experts and young scientists from various breakthrough scientific Read full announcement here. Rare Disease Day at NIH 2023 Tuesday, February 28, 2023, 9:00am to 5:00pm (registration required) NIH Natcher Conference Center (Building 45) Rare Disease Day takes place worldwide, typically on or near the last day of February each year, to raise awareness among policymakers and the public about rare diseases and their The 2023 virtual event is hosted in partnership between CHOC and UCI, together, we will foster new perspectives, ideas, and research collaborations to accelerate , Continue reading "The 2nd Annual CHOC and UCI Rare Disease Symposium & Family Conference", NORD Wisconsin Rare Action Network Rare Disease Day Saturday, March 11, 2023 Evjue Commons space at Olbrich Botanical Gardens 3330 Atwood Ave, Madison, WI 53704 Event is from 1:00pm -3:00 pm There is no cost to participants to attend this event One of the greatest challenges individuals living with a rare disease, their families, and , Continue reading "Wisconsin Rare Disease Day", NORD Iowa Rare Action Network Rare Disease Day Saturday, March 11, 2023 This is a virtual event. Presentations. Your meeting registration confirmation will include a link to generate a customized letter of invitation, which can be used when applying for a visa. Join our mailing list to receive exclusive content and offers. Click here to access the Guide for Authors or to Submit Your Paper. This organization dedicated to bringing together a significant number of diverse scholarly events for presentation within the conference program. Copyright 2023 NORD National Organization for Rare Disorders, Inc. All rights reserved. WebRare Diseases Meet 2023 provides a premier interdisciplinary platform for researchers to present the latest research findings and describe emerging technologies, and directions in rare diseases and orphan drugs issues. WebInternational Conference on Rare Diseases 2023. Illinois Rare Disease Day at the capital brings together rare disease advocates from across the state to make , Continue reading "2023 Illinois Rare Disease Day at the Capital". This symposium is designed to help researchers and clinicians to better manage and understand diagnostic options for patients with lysosomal diseases, identify areas requiring additional basic and clinical research, public policy and regulatory attention, and identify the latest findings in the natural history of lysosomal diseases. Conferences, and Present and discuss your plans, activities and products. This year conference will comprises of major sessions designed to offer comprehensive sessions that address current issues in various field of RARE DISEASES. If you would like to find out more about how we manage your personal information please see our privacy policy. Jaguar Health, Inc. By Hangin Out. Workshops, Public meeting: FDA Rare Disease Day 2023, An official website of the United States government, : Google Calendar. With a focus on the most critical topics, including accelerated approval, newborn screening, and equitable access to care, the 2023 NORD Summit promises a full program of productive discussions and collaborative solutions. Led by 60+ expert speakers and together with your peers, , Continue reading "Rare Disease Innovation & Partnership Summit", The first ever wAIHA Warriors Annual Patient Meeting will take place from March 24-26, 2023, in New Orleans. Christines work at Cure GM1 has involved a broad range, including animal models, biomarkers, gene therapy, enzyme replacement therapy, patient registries, patient reported outcomes, newborn screening and the first-ever GM1 caregiver preferences study. , Continue reading "Skate Under the Stars: A Rare Disease Celebration". MA 02199 We are always looking for ambitious people to join our team. Overseas, July and August brought EMA approvals for PTC Therapeutics'Upstaza and BioMarins Roctavian, the first gene therapies for AADC deficiency and Haemophilia A respectively. Rare Disease Therapies Development IL, Virtual Summit. By App. How are you raising awareness for the rare community this Rare Disease Day? Read full announcement here. 55 Kenosia Avenue The International Research Conference Aims and Objectives. Bring together a broad audience including patients, patient advocates, caregivers, health care providers, researchers, trainees, students, industry representatives and government staff. By continuing to use this website, we assume you agree to our, Click Here to Register or Modify Your Registration. WebRare Disease Conference 2023 - Rare Disease Innovation & Partnership Summit informaconnect.com E:info@hansonwade.com, Sheraton Boston Hotel Jaguar Health to Present at BioTrinity 2023 Conferences R&D Contribute to driving and directing the fast growing field of Health. Web3RD INTERNATIONAL RARE DISEASES CONFERENCE 2023: GREEK CHAPTER Mar 6 March 6 - March 8. Rare Disease West Michigan - Events | Calvin University http://ow.ly/5Wzs50Lj6CJ #NORDSummit. 2018 Challenge Details, NCATS Rare Diseases Are Not Rare! Public meeting: FDA Rare Disease Day 2023 - 02/27/2023 | FDA This website uses cookies to improve your experience. The WORLD CONGRESS ON RARE DISEASES - 2023, - An International Conference by BioGenesis Health Cluster is among the Worlds leading RARE DISEASE Conferences. Roscoe O. Brady Award Speaker: William A. Gahl, MD, PhD , Basic Science, Translational Research, ClinicalApplications, Contemporary Forum, and Late-Breaking Sessions, Emerging Trends: State-of the-Art for Experts, 2023 Scientific Sessions, ePosters and Satellite Symposia are available On Demand until. Congratulations! Research led by NCATS suggests that nationwide medical costs for individuals with rare diseases are likely as high as those faced by people with common diseases, such as cancer and heart failure. Distribution of exhibitor prospectus and support opportunities to all prior supporting companies, and also available by request. In all, nearly 10% of the U.S. population have a rare disease. Suite 310 Challenges faced by lay professionals in the community, Certificates will be provided to all speakers, delegates and students, Opportunity to meet worlds renowned at this event, Keynote forums by Prominent Physicians & Professors, Best platform for Global business and networking opportunities, Oral/Poster presentations by Young Researchers. The World Orphan Drug Congress USA is a place where innovation and expertise is showcased, solutions are found and learning is done. Connect, exchange with clinicians and health policy makers. Join the National Organization for Rare Disorders (NORD) October 15-17, 2023 for the Rare Diseases and Orphan Products Breakthrough Summit. 2020 Challenge Details, Translational Science Education & Training, Translational Science Training at Partner Institutions, Translational Science Training and Education Resources, Drug Discovery, Development and Deployment Maps, Assay Development and Screening Technology (ADST), Bridging Interventional Development Gaps (BrIDGs), Discovering New Therapeutic Uses for Existing Molecules, Genetic and Rare Diseases Information Center (GARD), A Specialized Platform for Innovative Research Exploration (ASPIRE), A Translational Approach to Addressing COVID-19, Clinical Trial Readiness for Rare Diseases, Disorders and Syndromes, Multidisciplinary Machine-Assisted, Genomic Analysis and Clinical Approaches to Shortening the Rare Diseases Diagnostic Odyssey, The Accelerating Medicines Partnership Bespoke Gene Therapy Consortium (BGTC), Cures Acceleration Network (CAN) Review Board, Division of Rare Diseases Research Innovation (DRDRI), access shareable resources to help raise awareness about rare diseases. Even after an accurate diagnosis, treatment often is not available because fewer than 500 rare diseases have FDA-approved treatments. Conference Rare Diseases THE BENEFITS PROVIDED TO THE ATTENDEES ARE: PARTICIPANTS - FIVE REASONS WHY I SHOULD ATTEND THE CONGRESS: PARTNERS - REASONS WHY I SHOULD EXHIBIT DURING THE CONGRESS: Copyright All rights reserved | Design & Developed by, Re-conceptualizing existing paradigms of diagnosis and difficulty, Breaking down silos how different models fit together. All Info for H.Res.181 - 118th Congress (2023-2024): Expressing support for the designation of February 28, 2023, as "Rare Disease Day". Prof Veronica Kinsler, Professor of Paediatric Dermatology and Dermatogenetics, Paul Nioi, Vice President, Discovery and Translational Research. (February 28, 2023) About Rare Disease Day Launched by EURORDIS-Rare Rare Diseases 2023 Connect and exchange with technology developers. Download the presentation, Panagiota MITROU, Deputy Head of the Autonomous Department of Therapeutic Protocols & Patient Registries, Ministry of Health Please note that NORD provides this information for the benefit of the rare disease community. Learn more about DRDRI and NCATS' rare diseases research programs and access shareable resources to help raise awareness about rare diseases. The goals of Rare Disease Day at NIH are to: Rare Disease Day at NIH was held at NIH Main Campus (Natcher Conference Center) on Tuesday, Feb. 28, 2023, from 9 a.m. to 5 p.m. EST. Third International Summit on Human Genome Editing Previous Events; Today Next Events; 1st International UAE Rare Disease Society Congress Feb 28 February 28 - March 1. Quincy, MA 02169 We use cookies to track usage and preferences. Vice President, Discovery and Translational Research. WebKatie Wise - EveryLife Foundation for Rare Diseases | Rare Disease Conference 2023 - Rare Disease Innovation & Partnership Summit Speaker Agenda Speakers Sponsors & Exhibitors Contact Katie Wise Young Adult Rare Representative at EveryLife Foundation for Rare Diseases Profile Kaitlyn (Kate) Wise grew up in Westchester, NY. FDA will host Rare Disease Day, a virtual public meeting, on February 27, 2023, 9:00 am 4:45 pm ET, in global observance of Rare Disease Week. Read more: https://bit.ly/3tGXzXn, Read the @RareDiseases Summit 2022 Recap! Participants can join in on a virtual walk/run to raise awareness for Rare disease day (wearing stripes!). Terrapinn is proud to be a member of isla. This years theme is Intersections with Rare Diseases A patient focused event.. The. The Lysosomal Disease Network (U54NS065768) is a part of the National Institutes of Health (NIH) Rare Diseases Clinical Research Network (RDCRN), supported through collaboration between the NIH Office of Rare Diseases Research (ORDR) at the National Center for Advancing Translational Science (NCATS), the National Institute of Neurological Disorders and Stroke (NINDS) and National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK). Use the conference hashtag #CrickRareDiseases. CME/CE/CEU credits are available for for select On Demand Scientific and Satellite Sessions. WebThe 2023 Gordon Research conference on Lysosomal Diseases will cover the latest discoveries that advance knowledge about basic lysosomal function; how exactly function is impaired in lysosomal diseases - and how they inform more universal application in Rare Disease Day at NIH aims to raise awareness about rare diseases, the people they affect, and NIH collaborations that address scientific challenges and advance research for new treatments. WebWorld Congress on Rare Diseases - 2023 +91 83102 90512 info@worldcongressonrarediseases.com About Conference The International Research Rare Disease Day at NIH will be held in person at NIH Main Campus (Natcher Conference Center) on Tuesday, Feb. 28, 2023, from 9 a.m. to 5 p.m. The event will be shared in multiple Facebook support groups for individuals specifically with PKU. Rare Disease National Heart, Lung, and Blood Institute, National Institute on Alcohol Abuse and Alcoholism, National Institute of Neurological Disorders and Stroke, Rare Diseases Clinical Research Networks Coalition of Patient Advocacy Groups. All comments must be identified with the docket number FDA-2022-N-3072-0001 through April 7, 2023. WebGT+R 2023 is a novel event, curating seasoned experts from across the gene therapy and rare disease therapeutic research and development industries. Rare Disease Crickresearchers are working at the forefront of the scientific response to answer some of the most urgent questions about the SARS-CoV-2 pathogen, from how we can improve testing, to why its deadly in some people but causes no symptoms in others. Office of Clinical Policy and Programs, Office of Orphan Products Development, More Meetings, We are a biomedical discoveryinstituteresearching the biologyunderlying human health. The goal of WORLDSymposium is to provide an interdisciplinary forum to explore and discuss specific areas of interest, research and clinical applicability related to lysosomal diseases. RE(ACT) Congress Presentations. WebInternational Conference on Rare Diseases 2023. How competent are lay professionals in addressing womens issues? 2023 WORLDSymposium is a medical education conference focused on lysosomal diseases. Each year, Global Genes convenes one of the worlds largest gatherings of rare disease patients, caregivers, advocates, healthcare professionals, Presentation will cover Jaguar and Napo Therapeutics' focus on development and commercialization of 13 - 14 September 2023 Princeton, New Jersey Register Why attend? November 1 December 1, 2022Late breaking abstract submission open. Hot off its heels we saw the accelerated approval of another bluebird bio product, Skysona. Phone: 202-588-5700. NORD is not a medical provider or health care facility and thus can neither diagnose any disease or disorder nor endorse or recommend any specific medical treatments. This conference is aimed at scientists, clinician scientists and doctors. Dates: February 24, 2023. How To Help A Family Member With Mental Illness, How School Affects Mental Health In High School Students, Empowering community members through mental health education, advocacy, and support, Effects of Financial Illiteracy on Physical, Mental, Emotional, Spiritual Health. Join our mailing lists to receive updates about our latest research and to hear about our free public events and exhibitions. Read full announcement here. Join the National Organization for Rare Disorders (NORD) October 15-17, 2023 for the Rare Diseases and Orphan Products Breakthrough Summit. Download the presentation, Magda CHLEBUS, Executive Director, Science Policy & Regulatory Affairs At EFPIA NORD is a registered 501(c)(3) charity organization. 06885462, with its registered office at 1 Midland Road, London NW1 1AT. WORLD is an acronym that stands for Were Organizing Research on Lysosomal Diseases. All Info for H.Res.181 - 118th Congress (2023-2024): Expressing support for the designation of February 28, 2023, as "Rare Disease Day". Location: Bartosza Gowackiego 35, Lublin, Poland. Congratulations to this years recipients! Come face to face with life-changing science, Engage and inspire with discovery science, The latest science and stories from the Crick, Working to discover the biology of health and disease. WORLDSymposiac/o GMI1900 NW Corporate BlvdSuite 410WBoca Raton, FL 33431. 2023 Discussions will focus on Webcast Information Download the presentation, International Conference on Rare Diseases 2023, Leveraging the momentum for a comprehensive rare disease strategy. NORD, along with its more than 300 patient organization members, is committed to the identification, treatment, and cure of rare disorders through programs of education, advocacy, research, and patient services. 2023 Conference Overcome Regulatory, Clinical, Manufacturing & Pricing Bottlenecks to Progress Safer, Efficacious, Accessible Rare Gene Therapies From Early Clinical Development Through to Approval, 2022 has been a landmark year for the global gene therapy space. With an expert speaking faculty devoted to bringing safer and more effective gene therapies to rare disease patients, key questions will be answered on how best the field can overcome regulatory, clinical, manufacturing and pricing bottlenecks to progress gene therapies into and through the clinic. How do lay professionals deal with issues around gender and sexuality in the community? Information on how to claim education credits is given only to registered attendees and is available in the 2023 WORLDSymposium mobile app. Rare Disease Day Conference | Events | Minor in Science and If you have problems viewing PDF files, download the latest version of Adobe Reader, For language access assistance, contact the NCATS Public Information Officer, National Center for Advancing Translational Sciences (NCATS), 6701 Democracy Boulevard, Bethesda MD 20892-4874 301-594-8966, U.S. Department of Health & Human Services, Clinical and Translational Science Awards (CTSA) Program, Rare Diseases Clinical Research Network (RDCRN), Therapeutics for Rare and Neglected Diseases (TRND), Additional Rare Diseases Research and Initiatives, Patient/Community Engagement & Health Information, Genetic and Rare Diseases Information Center, NCATS Toolkit for Patient-Focused Therapy Development, National COVID Cohort Collaborative (N3C), About NCATS Role in the NIH HEAL Initiative, Accelerating the Translation of Novel Compounds Toward INDs for Subsequent Clinical Testing, Fiscal Year 2019 Funded Projects and Prizes, NIH HEAL Initiative Funding & Collaboration Opportunities Led by NCATS, NCATS Program-Specific Funding Information, Prior NIH Approval of Human Subjects Research Frequently Asked Questions, NCATS Challenges and Prize Competitions Program, Bias Detection Tools in Health Care Challenge, LitCoin Natural Language Processing (NLP) Challenge, NCATS Rare Diseases Are Not Rare! Rare Disease Conferences 2023/2024/2025 will bring speakers from Asia, Africa, North America, South America, Antarctica, Europe, and Australia. Please enable JavaScript in your web browser to get the best experience. 1779 Massachusetts Avenue WebAll MassBio events adhere to our conference Diversity Policy and Anti-Harassment Policy. People loved the speakers, the timely topics, the exhibit hall, and networking opportunities. Rare Disease Day | 03-24-2023 05:00 PM | Quinnipiac Events Web8th International Conference on Rare Diseases and Orphan Drugs Osaka, Japan November 13-14, 2023 6th International Conference on Tropical and Infectious Diseases Bali, Indonesia December 07-08, 2023 6th Pathology and Infectious Disease Conference Prague, Czech Republic December 14-15, 2023 13th European Epidemiology and Public Phone: 617-249-7300, Danbury, CT office By Facilitated Meetings. Download the presentation, Antonis KATTAMIS, Professor of Pediatric Hematology-Oncology, President, Hellenic Society of Pediatric Hematology-Oncology With August came the green light for, As the gene therapy field continues to break records, there are still significant challenges to overcome relating to safety, efficacy, and accessibility. Summary. 4 min read. Leveraging the momentum for a comprehensive rare disease strategy Introductory Speech: An Applications for the 2023 PhD programme are open! WebHome | Leading Rare Diseases Conference | Orphan Disease Conferences | Orphan-Drugs Meetings May 25-26, 2023 10:00 AM GMT London, UK 4th International Conference on Rare Diseases and Orphan Drugs Pioneering Breakthroughs on Rare Diseases 83 : days 02 : Hours 59 : Mins 55 Secs Brochure Download Advertising Webinars Rare Disease Day at NIH 2023 | National Center for Advancing Join us for three days in February 21, 2023: Robert J. Gorlin Symposium and Emerging Trends February 22-26, 2023: Research Meeting Hilton Orlando, Orlando, FL, USA Scientific This will coordinate appears, disperse information, and meet with recurring pattern and potential investigators and get name affirmation at First Virtual Conference. Expert speakers from across the UK Rare Diseases community will present their latest research. About Rare Disease Day . October 15-17, 2023 Congratulations to Christine Waggoner, the recipient of the WORLDSymposium 2023 Patient Advocate Leader (PAL) Award.